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dc.contributor.authorHawkins, P. N.
dc.contributor.authorSolomon, S. D.
dc.contributor.authorPolydefkis, M.
dc.contributor.authorDyck, P. J.
dc.contributor.authorYang, C. -C.
dc.contributor.authorUeda, M.
dc.contributor.authorKristen, A. V.
dc.contributor.authorTournev, I.
dc.contributor.authorSchmidt, H. H.
dc.contributor.authorCoelho, T.
dc.contributor.authorBerk, J. L.
dc.contributor.authorLin, K. -P.
dc.contributor.authorVita, G.
dc.contributor.authorAttarian, S.
dc.contributor.authorPlante-Bordeneuve, V.
dc.contributor.authorMezei, M. M.
dc.contributor.authorCampistol, J. M.
dc.contributor.authorBuades, J.
dc.contributor.authorBrannagan, T. H.
dc.contributor.authorKim, B. J.
dc.contributor.authorOh, J.
dc.contributor.authorGandhi, P. J.
dc.contributor.authorGoyal, S.
dc.contributor.authorChen, J.
dc.contributor.authorStrahs, A. L.
dc.contributor.authorNochur, S. V.
dc.contributor.authorSweetser, M. T.
dc.contributor.authorGarg, P. P.
dc.contributor.authorVaishnaw, A. K.
dc.contributor.authorGollob, J. A.
dc.contributor.authorSuhr, O. B.
dc.contributor.authorParman, Y.
dc.contributor.authorSekijima, Y.
dc.contributor.authorAdams, D.
dc.contributor.authorGonzalez-Duarte, A.
dc.contributor.authorO'Riordan, W. D.
dc.date.accessioned2021-03-03T13:39:06Z
dc.date.available2021-03-03T13:39:06Z
dc.date.issued2018
dc.identifier.citationAdams D., Gonzalez-Duarte A., O'Riordan W. D. , Yang C. -. , Ueda M., Kristen A. V. , Tournev I., Schmidt H. H. , Coelho T., Berk J. L. , et al., "Patisiran, an RNAi Therapeutic, for Hereditary Transthyretin Amyloidosis", NEW ENGLAND JOURNAL OF MEDICINE, cilt.379, sa.1, ss.11-21, 2018
dc.identifier.issn0028-4793
dc.identifier.othervv_1032021
dc.identifier.otherav_35423c86-a8ae-45b1-b3c8-d28439809b09
dc.identifier.urihttp://hdl.handle.net/20.500.12627/39999
dc.identifier.urihttps://doi.org/10.1056/nejmoa1716153
dc.description.abstractBACKGROUND
dc.language.isoeng
dc.subjectKlinik Tıp
dc.subjectKlinik Tıp (MED)
dc.subjectTıp
dc.subjectSağlık Bilimleri
dc.subjectTemel Tıp Bilimleri
dc.subjectTIP, GENEL & İÇECEK
dc.titlePatisiran, an RNAi Therapeutic, for Hereditary Transthyretin Amyloidosis
dc.typeMakale
dc.relation.journalNEW ENGLAND JOURNAL OF MEDICINE
dc.contributor.departmentShinshu University , ,
dc.identifier.volume379
dc.identifier.issue1
dc.identifier.startpage11
dc.identifier.endpage21
dc.contributor.firstauthorID254883


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